Skip to main content
Figure 4 | Skeletal Muscle

Figure 4

From: Immortalized pathological human myoblasts: towards a universal tool for the study of neuromuscular disorders

Figure 4

Antisense oligonucleotides (AONs) tested in immortalized cells for exon-skipping pre-clinical studies. (A) Validation of AO51 efficacy for exon 51 skipping on primary (Prim.; Duchenne muscular dystrophy (DMD)) and immortalized cultures of a Δ48-50 patient with DMD. (B) Evaluation of the efficacy of various AONs on control immortalized cells targeting exons 17 and 18.

Back to article page

Skeletal Muscle

ISSN: 2044-5040

Contact us